Clinical Trials List
2022-09-01 - 2026-05-18
Phase III
Recruiting1
ICD-10E75.21
Fabry (-Anderson) disease
ICD-10E75.22
Gaucher disease
ICD-10E75.240
Niemann-Pick disease type A
ICD-10E75.241
Niemann-Pick disease type B
ICD-10E75.242
Niemann-Pick disease type C
ICD-10E75.243
Niemann-Pick disease type D
ICD-10E75.248
Other Niemann-Pick disease
ICD-10E75.249
Niemann-Pick disease, unspecified
ICD-10E75.3
Sphingolipidosis, unspecified
ICD-10E77.0
Defects in post-translational modification of lysosomal enzymes
ICD-10E77.1
Defects in glycoprotein degradation
ICD-10E77.8
Other disorders of glycoprotein metabolism
ICD-10E77.9
Disorder of glycoprotein metabolism, unspecified
ICD-9272.7
Lipidoses
-
Trial Applicant
-
Sponsor
-
Trial scale
Multi-Regional Multi-Center
-
Update
2026/02/01
Investigators and Locations
Co-Principal Investigator
- Tiffany Ting-Fang Shih Division of Radiology
- Yin-Hsiu Chien Division of General Internal Medicine
- CHIN-HSIEN LIN Division of Neurology
- 彭信逢 Division of Radiology
- 周書緯 Division of Pediatrics
- Ta-Ching Chen Division of Ophthalmology
- WUH-LIANG HWU Division of Pediatrics
The Actual Total Number of Participants Enrolled
0 Recruiting
Condition/Disease
Objectives
Test Drug
Active Ingredient
Dosage Form
Dosage
Endpoints
Inclution Criteria
The Estimated Number of Participants
-
Taiwan
2 participants
-
Global
ˋ40 participants
