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Clinical Trials List

Protocol NumberPTC124-GD-041-DMD
Completed

2017-09-01 - 2021-12-31

Phase III

Recruiting2

ICD-10G71.0

Muscular dystrophy

  • Trial Applicant

    MEDPACE TAIWAN LIMITED

  • Sponsor

  • Trial scale

    Multi-Regional Multi-Center

  • Update

    2026/04/01

Investigators and Locations

Principal Investigator WANG-TSO LEE Division of Pediatrics

Co-Principal Investigator

The Actual Total Number of Participants Enrolled

0 Recruiting

Audit

None

Principal Investigator Yuh-Jyh Jong Division of Pediatrics

Co-Principal Investigator

The Actual Total Number of Participants Enrolled

0 Recruiting

Condition/Disease

Objectives

Test Drug

Active Ingredient

Dosage Form

Dosage

Endpoints

Inclution Criteria

The Estimated Number of Participants

  • Taiwan

    11~16 participants

  • Global

    340 participants