Clinical Trials List
Protocol NumberPTC124-GD-041-DMD
Completed
2017-09-01 - 2021-12-31
Phase III
Recruiting2
ICD-10G71.0
Muscular dystrophy
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Trial Applicant
MEDPACE TAIWAN LIMITED
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Sponsor
-
Trial scale
Multi-Regional Multi-Center
-
Update
2026/04/01
Investigators and Locations
Co-Principal Investigator
- 王麗君 Division of Pediatrics
- WEN-CHIN WENG Division of Pediatrics
The Actual Total Number of Participants Enrolled
0 Recruiting
Audit
None
Co-Principal Investigator
- 徐仲豪 Division of Pediatrics
- Wen-Chen Liang Division of Pediatrics
The Actual Total Number of Participants Enrolled
0 Recruiting
Condition/Disease
Objectives
Test Drug
Active Ingredient
Dosage Form
Dosage
Endpoints
Inclution Criteria
The Estimated Number of Participants
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Taiwan
11~16 participants
-
Global
340 participants