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Division of Pediatrics
更新時間:2023-09-19
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徐仲豪
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2020-05-01 - 2026-12-31
Condition/Disease
spinal muscular atrophy
Test Drug
Risdiplam
Participate Sites1Sites
Recruiting1Sites
2020-10-30 - 2039-12-04
Duchenne Muscular Dystrophy
PF-06939926
Participate Sites3Sites
Recruiting3Sites
2017-09-01 - 2023-12-29
Participate Sites2Sites
Terminated2Sites
2015-01-26 - 2025-06-02
2020-04-01 - 2026-09-30
Recruiting2Sites
2021-04-01 - 2027-01-30
2024-07-01 - 2029-08-31
Not yet recruiting2Sites
2022-03-01 - 2024-09-30
2021-11-01 - 2026-02-09
Patients aged 2 to under 18 years with treatment-naïve, late-onset type 2 spinal muscular atrophy (SMA) who are able to sit but have never walked.
OAV101
Not yet recruiting1Sites
Study ended1Sites
2019-08-31 - 2024-06-03
Eteplirsen
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