Clinical Trials List
2023-09-15 - 2026-12-15
Phase IV
Recruiting2
ICD-10E75.21
Fabry (-Anderson) disease
ICD-10E75.22
Gaucher disease
ICD-10E75.240
Niemann-Pick disease type A
ICD-10E75.241
Niemann-Pick disease type B
ICD-10E75.242
Niemann-Pick disease type C
ICD-10E75.243
Niemann-Pick disease type D
ICD-10E75.248
Other Niemann-Pick disease
ICD-10E75.249
Niemann-Pick disease, unspecified
ICD-10E75.3
Sphingolipidosis, unspecified
ICD-10E77.0
Defects in post-translational modification of lysosomal enzymes
ICD-10E77.1
Defects in glycoprotein degradation
ICD-10E77.8
Other disorders of glycoprotein metabolism
ICD-10E77.9
Disorder of glycoprotein metabolism, unspecified
ICD-9272.7
Lipidoses
-
-
Trial Applicant
Johnson & Johnson
-
Sponsor
-
-
Trial scale
Taiwan Multiple Center
-
Update
2026/09/11
Investigators and Locations
Co-Principal Investigator
The Actual Total Number of Participants Enrolled
0 Recruiting
Co-Principal Investigator
The Actual Total Number of Participants Enrolled
0 Recruiting
Study Contacts
- -
Condition/Disease
Objectives
Test Drug
Active Ingredient
Dosage Form
Dosage
Endpoints
Inclution Criteria
Exclusion Criteria
The Estimated Number of Participants
-
Taiwan
5 participants
-
Global
5 participants