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TPIDB > Principal Investigator

Principal Investigator


National Taiwan University Hospital (在職)

Division of Pediatrics

Division of General Internal Medicine

更新時間:2023-09-19

胡務亮HWU, WUH-LIANG
  • Principal Investigator
  • Clinical Trial Experience (year) 17 years 9 個月

篩選

List

40Cases

2022-03-01 - 2024-09-30

Phase III

Completed
  • Condition/Disease

  • Test Drug

Participate Sites
2Sites

Recruiting2Sites

2022-06-01 - 2026-12-31

Phase III

Active
  • Condition/Disease

  • Test Drug

Participate Sites
1Sites

Recruiting1Sites

2021-11-01 - 2026-02-09

Phase III

Completed
A Randomized, Sham-controlled, Double-blind Study to Evaluate the Efficacy and Safety of Intrathecal OAV101 in Type 2 Spinal Muscular Atrophy (SMA) Patients Who Are ≥ 2 to < 18 Years of Age, Treatment Naive, Sitting, and Never Ambulatory
  • Condition/Disease

    Patients aged 2 to under 18 years with treatment-naïve, late-onset type 2 spinal muscular atrophy (SMA) who are able to sit but have never walked.

  • Test Drug

    OAV101

Participate Sites
2Sites

Not yet recruiting1Sites

Study ended1Sites

2021-09-30 - 2023-08-01

Phase III

Completed
A Phase IIIb, open-label, single-arm, single-dose, multicenter study to evaluate the safety, tolerability and efficacy of gene replacement therapy with intravenous OAV101 (AVXS-101) in pediatric patients with spinal muscular atrophy (SMA)
  • Condition/Disease

    Pediatric patients with spinal muscular atrophy (SMA)

  • Test Drug

    OAV101

Participate Sites
2Sites

Recruiting1Sites

Study ended1Sites

2023-01-10 - 2031-02-26

Phase IV

Active
  • Condition/Disease

  • Test Drug

Participate Sites
2Sites

Recruiting2Sites

2023-12-01 - 2028-06-30

Phase III

Active
  • Condition/Disease

  • Test Drug

Participate Sites
2Sites

Recruiting2Sites

2017-03-30 - 2025-02-20

Phase III

Active
Morquio A registry Study
  • Condition/Disease

    Mucopolysaccharidosis type IVA

  • Test Drug

    Vimizim

Participate Sites
12Sites

Not yet recruiting8Sites

Recruiting2Sites

Terminated2Sites

2022-02-01 - 2028-07-31

Phase II

Active
  • Condition/Disease

  • Test Drug

Participate Sites
1Sites

Recruiting1Sites

1 2 3 4