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Clinical Trials List

Protocol NumberACE-536-LTFU-001
Completed

2019-08-01 - 2025-04-30

Phase III

Terminated3

ICD-10D56.0

Alpha thalassemia

ICD-10D56.1

Beta thalassemia

ICD-10D56.2

Delta-beta thalassemia

ICD-10D56.3

Thalassemia minor

ICD-10D56.5

Hemoglobin E-beta thalassemia

ICD-10D56.8

Other thalassemias

ICD-10D56.9

Thalassemia, unspecified

ICD-10D57.40

Sickle-cell thalassemia without crisis

ICD-10D57.411

Sickle-cell thalassemia with acute chest syndrome

ICD-10D57.412

Sickle-cell thalassemia with splenic sequestration

ICD-10D57.419

Sickle-cell thalassemia with crisis, unspecified

ICD-9282.4

Thalassemias

  • Sponsor

  • Trial scale

    Multi-Regional Multi-Center

  • Update

    2026/02/01

Investigators and Locations

Principal Investigator CHING-TIEN PENG Division of Pediatrics

Co-Principal Investigator

The Actual Total Number of Participants Enrolled

0 Terminated

Principal Investigator Yi-Chang Liu Division of Hematology & Oncology

Co-Principal Investigator

The Actual Total Number of Participants Enrolled

0 Terminated

Principal Investigator MENG-YAO LU Division of Pediatrics

Co-Principal Investigator

The Actual Total Number of Participants Enrolled

0 Terminated

Condition/Disease

Objectives

Test Drug

Active Ingredient

Dosage Form

Dosage

Endpoints

Inclution Criteria

The Estimated Number of Participants

  • Taiwan

    10 participants

  • Global

    700 participants