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Clinical Trials List

Protocol NumberC0371003

2022-07-01 - 2023-03-16

Others

Recruiting2

ICD-10D67

Hereditary factor IX deficiency

ICD-9286.1

Congenital factor IX disorder

xxxxxx

  • Sponsor

    xxxxxx

  • Trial scale

    Multi-Regional Multi-Center

  • Update

    2025/11/13

Investigators and Locations

Principal Investigator 沈銘鏡

Co-Principal Investigator

The Actual Total Number of Participants Enrolled

0 Recruiting

Principal Investigator JIAAN-DER WANG

Co-Principal Investigator

The Actual Total Number of Participants Enrolled

0 Recruiting

Condition/Disease

xxxxxx

Objectives

xxxxxx

Test Drug

PF-06838435 (Fidanacogene elaparvovec)

Active Ingredient

PF-06838435 (Fidanacogene elaparvovec)

Dosage Form

Solution for infusion

Dosage

1.00E+13 vg/mL

Endpoints

xxxxxx

Inclution Criteria

xxxxxx

Exclusion Criteria

xxxxxx

The Estimated Number of Participants

  • Taiwan

    2 participants

  • Global

    24 participants