Clinical Trials List
Protocol NumberC0371003
2022-07-01 - 2023-03-16
Others
Recruiting2
ICD-10D67
Hereditary factor IX deficiency
ICD-9286.1
Congenital factor IX disorder
xxxxxx
-
Sponsor
xxxxxx
-
Trial scale
Multi-Regional Multi-Center
-
Update
2025/11/13
Investigators and Locations
The Actual Total Number of Participants Enrolled
0 Recruiting
The Actual Total Number of Participants Enrolled
0 Recruiting
Condition/Disease
xxxxxx
Objectives
xxxxxx
Test Drug
PF-06838435 (Fidanacogene elaparvovec)
Active Ingredient
PF-06838435 (Fidanacogene elaparvovec)
Dosage Form
Solution for infusion
Dosage
1.00E+13 vg/mL
Endpoints
xxxxxx
Inclution Criteria
xxxxxx
Exclusion Criteria
xxxxxx
The Estimated Number of Participants
-
Taiwan
2 participants
-
Global
24 participants