Clinical Trials List
2017-03-30 - 2025-02-20
Phase III
Not yet recruiting8
Recruiting2
Terminated2
ICD-10E76.01
Hurler's syndrome
ICD-10E76.02
Hurler-Scheie syndrome
ICD-10E76.03
Scheie's syndrome
ICD-10E76.1
Mucopolysaccharidosis, type II
ICD-10E76.210
Morquio A mucopolysaccharidoses
ICD-10E76.211
Morquio B mucopolysaccharidoses
ICD-10E76.219
Morquio mucopolysaccharidoses, unspecified
ICD-10E76.22
Sanfilippo mucopolysaccharidoses
ICD-10E76.29
Other mucopolysaccharidoses
ICD-10E76.3
Mucopolysaccharidosis, unspecified
ICD-10E76.8
Other disorders of glucosaminoglycan metabolism
ICD-10E76.9
Glucosaminoglycan metabolism disorder, unspecified
ICD-9277.5
Mucopolysaccharidosis
Morquio A registry Study
-
Trial Applicant
ICON Clinical Research Pte Ltd
-
Sponsor
BioMarin Pharmaceutical Inc.
-
Trial scale
Multi-Regional Multi-Center
-
Update
2026/02/01
Investigators and Locations
Co-Principal Investigator
- 林翔宇 Division of Pediatrics
The Actual Total Number of Participants Enrolled
0 Not yet recruiting
Co-Principal Investigator
- 陳冠容 Division of Pediatrics
The Actual Total Number of Participants Enrolled
0 Not yet recruiting
Co-Principal Investigator
- 柯瑜媛 Division of Pediatrics
The Actual Total Number of Participants Enrolled
0 Not yet recruiting
Co-Principal Investigator
The Actual Total Number of Participants Enrolled
0 Not yet recruiting
Co-Principal Investigator
The Actual Total Number of Participants Enrolled
0 Not yet recruiting
Co-Principal Investigator
The Actual Total Number of Participants Enrolled
0 Not yet recruiting
Co-Principal Investigator
- WUH-LIANG HWU Division of Pediatrics
The Actual Total Number of Participants Enrolled
0 Not yet recruiting
Co-Principal Investigator
The Actual Total Number of Participants Enrolled
0 Not yet recruiting
Co-Principal Investigator
- 蔡孟哲 Division of Pediatrics
The Actual Total Number of Participants Enrolled
0 Recruiting
Co-Principal Investigator
The Actual Total Number of Participants Enrolled
0 Stop recruiting
Co-Principal Investigator
- 林翔宇 Division of Pediatrics
The Actual Total Number of Participants Enrolled
0 Stop recruiting
Co-Principal Investigator
The Actual Total Number of Participants Enrolled
0 Recruiting
Condition/Disease
Objectives
Test Drug
Active Ingredient
Dosage Form
Dosage
Endpoints
-natural course, physical examination and biochemical data
-long ter safty and averse events
-efficacy
Inclution Criteria
Exclusion Criteria
The Estimated Number of Participants
-
Taiwan
16 participants
-
Global
520 participants