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Clinical Trials List

Protocol NumberAT1001-012

2011-06-01 - 2015-02-28

Phase III

Terminated1

ICD-10E75.21

Fabry (-Anderson) disease

ICD-10E75.22

Gaucher disease

ICD-10E75.240

Niemann-Pick disease type A

ICD-10E75.241

Niemann-Pick disease type B

ICD-10E75.242

Niemann-Pick disease type C

ICD-10E75.243

Niemann-Pick disease type D

ICD-10E75.248

Other Niemann-Pick disease

ICD-10E75.249

Niemann-Pick disease, unspecified

ICD-10E75.3

Sphingolipidosis, unspecified

ICD-10E77.0

Defects in post-translational modification of lysosomal enzymes

ICD-10E77.1

Defects in glycoprotein degradation

ICD-10E77.8

Other disorders of glycoprotein metabolism

ICD-10E77.9

Disorder of glycoprotein metabolism, unspecified

ICD-9272.7

Lipidoses

  • Trial Applicant

    IQVIA RDS Taiwan Ltd.

  • Sponsor

  • Trial scale

    Multi-Regional Multi-Center

  • Update

    2025/08/20

Investigators and Locations

Principal Investigator Dau-Ming Niu Division of Pediatrics

Co-Principal Investigator

The Actual Total Number of Participants Enrolled

0 Terminated

Condition/Disease

Objectives

Test Drug

Active Ingredient

Dosage Form

Dosage

Endpoints

Inclution Criteria

The Estimated Number of Participants

  • Taiwan

    2-4 participants

  • Global

    60 participants